Official Title: A randomised, double blind, placebo controlled, multicentre study to evaluate the efficacy and safety of Givinostat in ambulant patients with Duchenne Muscular Dystrophy (DMD) (DSC/14/2357/48).
EPIDYS: epigenetic rescue of dystrophin dysfunction.
Purpose: The main objective of this study is to evaluate the efficacy of Givinostat compared to placebo to slow the disease progression in Duchenne Muscular Dystrophy (DMD) ambulant patients. Additional objectives include evaluation of safety, and tolerability of the drug.
Location: Europe (Belgium, France, Germany, Italy, Netherlands, Spain and UK) and North America (Canada and US).
For more information and enrollment status, please visit www.clinicaltrials.gov (ClinicalTrials.gov Identifier: NCT02851797) or https://www.clinicaltrialsregister.eu/ctr-search/search.